Joseph Penrod was diagnosed with Duchenne muscular dystrophy when he was 5 years old.
Although a diagnosis can be overwhelming, and a disease of this magnitude can begin to define a child, Joseph has led the way with a positive attitude and a love of life. Hope for Joseph and all the other children with Duchenne is fueled by a mom on a mission and an army of committed volunteers who will not quit until the day there is a cure.
Investigators: Jeff Chamberlain, PhD; Ron Berenson, MD; and Michael Regnier, PhD.
Relaxin is a natural hormone, which has a number of biological effects that may be of benefit in Duchenne Muscular Dystrophy (DMD), including its ability to regenerate muscle, reduce scarring and improve cardiac function. […]
Duchenne is characterized by muscle degeneration resulting in progressive weakness and, ultimately, heart and respiratory failure. Muscle stem cells called satellite cells can foster the regeneration of diseased muscle in DMD, but studies show that satellite cell populations become exhausted over time. […]
HT-100 is a delayed-response form of halofuginone hydrobromide, a derivative of a natural compound found in a species of plant. The drug is being developed for Duchenne by Massachusetts-based Halo Therapeutics, LLC […]